Unravelling endogenous MicroRNAs system dysfunction as a new pathophysiological mechanism in Machado-Joseph disease

”Unravelling endogenous MicroRNAs system dysfunction as a new pathophysiological mechanism in Machado-Joseph disease” has been accepted for publication in Molecular Therapy. This work was supported in part by JPND through the SynSpread, ESMI and ModelPolyQ projects.